Adeno-associated virus vectors for human gene therapy
The AAV vector toolkit: poised at the clinical crossroads. - Abstract - Europe PMC
VIRAL DELIVERY OF GDNF PROMOTES FUNCTIONAL INTEGRATION OF HUMAN STEM CELL GRAFTS IN PARKINSON'S DISEASE | bioRxiv
Adeno-associated virus vectors for human gene therapy
A novel adeno-associated virus capsid with enhanced neurotropism corrects a lysosomal transmembrane enzyme deficiency
Efficient intracerebral delivery of AAV5 vector encoding human ARSA in non-human primate
PDF) AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington's Disease Minipig Model
Adeno-associated virus vectors for human gene therapy
Science Magazine - November 29, 2019 - Median raphe controls acquisition of negative experience in the mouse
Pattern of transport of AAV5-hM4D(Gi)-mCherry following injections in... | Download Scientific Diagram
WO2020172490A1 - Recombinant adeno-associated virus for treatment of grn-associated adult-onset neurodegeneration - Google Patents
Surface Loop Dynamics in Adeno-Associated Virus Capsid Assembly | Journal of Virology
Best of most possible worlds: Hybrid gene therapy vectors based on parvoviruses and heterologous viruses: Molecular Therapy
WO2020172490A1 - Recombinant adeno-associated virus for treatment of grn-associated adult-onset neurodegeneration - Google Patents
Relevance of Assembly-Activating Protein for Adeno-associated Virus Vector Production and Capsid Protein Stability in Mammalian and Insect Cells | Journal of Virology
Generation of Cell Lines Capable of Producing High-titer Viral Stocks for Use in Vaccine Manufacture and Gene Therapy | ATCC
Generation of Cell Lines Capable of Producing High-titer Viral Stocks for Use in Vaccine Manufacture and Gene Therapy | ATCC
Terminal N-Linked Galactose Is the Primary Receptor for Adeno-associated Virus 9* - Journal of Biological Chemistry
Role of VTA dopamine neurons and neuroligin 3 in sociability traits related to nonfamiliar conspecific interaction | Nature Communications
AlphaLISA AAV5 Capsid Detection Kit, 100 Assay Points | PerkinElmer
WO2020172490A1 - Recombinant adeno-associated virus for treatment of grn-associated adult-onset neurodegeneration - Google Patents
Translation of MicroRNA-Based Huntingtin-Lowering Therapies from Preclinical Studies to the Clinic: Molecular Therapy
Restoring brain cholesterol turnover improves autophagy and has therapeutic potential in mouse models of spinocerebellar ataxia
Cross-Packaging of a Single Adeno-Associated Virus (AAV) Type 2 Vector Genome into Multiple AAV Serotypes Enables Transduction w
Synthetically Engineered Adeno-Associated Virus for Efficient, Safe, and Versatile Gene Therapy Applications | ACS Nano
